Forbes contributors publish independent expert analyses and insights. Spinal muscular atrophy affects the nerves that control muscle movement, leading to progressive weakening. As a result, infants ...

A Fort Worth toddler was the first person in Texas to be treated with a new, high-dose drug for a rare genetic disorder.

Former Little Mix star has been campaigning for newborn babies to be screened for the rare condition, which causes ...

Spinal muscular atrophy (SMA) is a genetic neuromuscular disease affecting specialized nerve cells that control voluntary muscle movement, according to the Muscular Dystrophy Association (MDA). It can ...

You might not think of diabetes when you think of muscle function. But a common diabetes drug that regulates blood sugar can also prevent muscle atrophy and muscular fibrosis—which can help the ...

Oral risdiplam (Evrysdi, Genentech) started in the first 6 weeks of life let most infants with presymptomatic spinal muscular atrophy (SMA) reach motor milestones typical of healthy babies, results of ...

An experimental study in Science Advances shows that statins, primarily fluvastatin in these experiments, may promote ...

Former Little Mix singer Jesy Nelson has described the roll-out of spinal muscular atrophy (SMA) screening as a “postcode ...

Spinal muscular atrophy (SMA) is a genetic, progressive neuromuscular disorder. SMA affects muscle-controlling nerve cells, called motor neurons, in the spinal cord. The condition leads to muscle ...

A new clinical trial has revealed encouraging results for a muscle-targeting therapy aimed at improving motor function in children and adolescents with spinal muscular atrophy, according to a study ...

Spinal muscular atrophy (SMA) and spina bifida are distinct conditions that affect the nerves that allow for voluntary motor control. Share on Pinterest press coverage photography/Getty Images SMA is ...