The teen's mother said he first began showing symptoms at 2 months old when “his arms and legs were just hanging by his side” ...

Basel, July 2, 2026 – Novartis today announced that the European Commission (EC) has approved Itvisma ® (onasemnogene ...

A student in Northern California didn’t let a rare disease stop him from graduating high school, attending classes with a telepresence robot, and marking a triumphant end to a unique academic journey.

Forbes contributors publish independent expert analyses and insights. Spinal muscular atrophy affects the nerves that control muscle movement, leading to progressive weakening. As a result, infants ...

Panelists discuss how spinal muscular atrophy is an autosomal recessive genetic disease affecting motor neurons with 3 currently approved disease-modifying therapies that restore SMN protein ...

Ancient bacteria that have evolved to become integral to our cells—converting nutrients from food into energy—may also contribute to neurologic disorders, such as spinal muscular atrophy (SMA) and ...

A young girl from Utah with Spinal Muscular Atrophy was named an honorary Monster Jam driver on Wednesday.

Jesy Nelson is sharing the moment no parent expects. And it is almost impossible to watch lightly. The former Little Mix ...

You might not think of diabetes when you think of muscle function. But a common diabetes drug that regulates blood sugar can also prevent muscle atrophy and muscular fibrosis—which can help the ...

Muscle loss is a well-publicized side effect of GLP-1 drugs, prompting a surge of interest in ingredients that can attenuate ...