Neurogene Inc. (Nasdaq: NGNE), a clinical-stage company founded to bring life-changing genetic medicines to patients and families affected by rare neurological diseases, today announced positive, ...
Rett syndrome is a rare neurodegenerative disorder that almost exclusively affects girls. It is typically diagnosed in babies ...
An expert discusses the current treatment landscape of Rett syndrome including the goals of treatment and implications for utilization management strategies with the disease. David Lieberman, MD, PhD: ...
Stifel 2025 Healthcare Conference November 12, 2025 4:40 PM ESTCompany ParticipantsRachel McMinn - Founder, Executive Chair ...
An expert explains how Rett syndrome is diagnosed, how commonly it is misdiagnosed, disease progression, and which providers are best positioned to manage a Rett Syndrome patient. David Lieberman, MD, ...
The SpartanNash YMCA of Greater Grand Rapids recently hosted an open-swim event as part of a newly-launched program called ...
Richard Engel, chief foreign correspondent for NBC News, announced on Thursday that his six-year-old son Henry had passed away from a rare neurological disorder. “Our beloved son Henry passed away,” ...
In commemoration of Rett syndrome awareness month this October, Acadia Pharmaceuticals is launching an awareness campaign to shine a light on patients' journeys and show that each person living with ...
Rett syndrome is a neurodevelopmental disorder that primarily affects girls, most of whom have mutations in the transcription regulatory gene MECP2. However, mutations in MECP2 also have been ...
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