Doctors at Cleveland Clinic used a one-time gene editing cell therapy to modify Danielle’s own blood-forming stem cells to ...

Caden Major was born with sickle cell disease – an inherited blood disorder affecting red blood cells. Now at 19 years old, ...

Major is one of the first pediatric patients in Florida to receive gene therapy for sickle cell disease since the FDA ...

For individuals living with sickle cell disease (SCD), the transition from pediatric to adult care can be one of the most ...

Motixafortide alone and in combination with natalizumab (VLA-4 inhibitor) led to robust hematopoietic stem cell (HSC) ...

Most people with sickle cell disease who undergo allogeneic hematopoietic cell transplantation achieve favorable long-term ...

Less than a third of ED visits for acute sickle cell disease pain were guideline-adherent for the timely administration of ...

Preliminary results from two trials of the gene therapy exagamglogene autotemcel (exa-cel) suggest the therapy offers an ...

A higher dose of the experimental pill for sickle cell disease showed more promise, Fulcrum said at the American Society of ...

Patients who underwent hematopoietic cell transplantation for sickle cell disease saw high rates of survival without disease ...

“To provide menstruating patients with sickle cell disease the best care, primary care physicians, gynecologists, and ...

Patients who underwent hematopoietic cell transplantation for sickle cell disease saw high rates of survival without disease ...