Individuals born with Usher syndrome type 1F do not have a sense of balance, cannot hear, and lose their vision over time. But scientists have now developed a gene therapy that could enable patients ...
LEIDEN, Netherlands & CAMBRIDGE, Mass., March 25, 2020 (GLOBE NEWSWIRE) -- ProQR Therapeutics N.V. (Nasdaq:PRQR), a company dedicated to changing lives through the creation of transformative RNA ...
Never miss an episode of Living Well with Alison Starling. Subscribe now on Apple Podcasts, Spotify or wherever you get your podcasts. Less than 1% of the world's population is believed to be living ...
The four-year study will inform clinical trial design for emerging USH3 therapies. Approximately 400,000 people around the world are affected by various types of Usher syndrome, the leading cause of ...
AAVantgarde Bio (AAVantgarde), a clinical-stage, biotechnology company pioneering therapies for inherited retinal diseases (IRDs), today announced the successful closing of a $141 million (€122 ...
A Chinese proverb states that a journey of a thousand miles begins with a single step. For Netherlands native Tim Schroeder, a very meaningful and intense journey of millions of pedals on his bicycle ...
NPI-001 shows more than 50% reduction in photoreceptor loss caused by RP associated with USH over two years NPI-001 was well tolerated, with no persistent drug-related adverse events Results were ...
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