There was a reduction in volume of involvement, cardiac pyrophosphate activity, native T1, and extracellular volume during a median of 369 days between scans in patients with ATTR-CM being treated.

Patients with ATTR-CM had significantly impaired global longitudinal strain and higher mechanical dispersion compared to their first-degree relatives who were not affected by the disease. Increased ...

Sickle cell disease is inherited in an autosomal recessive pattern, which means that a child is born with SCD only when they inherit 2 defective copies of the sickle cell gene (1 from each parent). If ...

Chronic inflammatory demyelinating polyneuropathy (CIDP) is a rare acquired autoimmune neurological disorder in which both T-cell-mediated and humoral immune mechanisms target healthy myelinated ...

Between 1970 and 1995, the incidence of new NHL cases increased. Between 2007 and 2016, new cases declined by approximately 0.9% per year, and mortality from NHL decreased by 2.2% per year. 3 ...

Several factors can contribute to the suppression of bone marrow erythropoiesis in infants with HDFN, including maternal antibodies, intrauterine transfusion, and simple transfusion. The suppression ...

Art Still is a former defensive end for the Kansas City Chiefs and an NFL Hall of Famer. Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Art Still, former defensive end for the ...

The highest in-hospital mortality and complication rates were found among Asian or Pacific Islander patients, and the longest hospital stays were found among African Americans and those classified as ...

Patients with PCNSL should be closely monitored for extracerebral relapses, including ocular. Primary central nervous system lymphoma (PCNSL) can recur as isolated ophthalmologic and isolated cerebral ...

Individuals with advanced liver disease may also experience significant weight loss due to nausea and poor appetite. Candidates for liver transplantation may need to gain weight to optimize surgical ...

Taylor Kane is executive director of Remember the Girls, a nonprofit group that advocates on behalf of females with X-linked disorders (Photo courtesy of Taylor Kane) New Jersey native Taylor Kane ...

Study results revealed a significantly lower rate of flares and a higher rate of remission among patients treated with inebilizumab. A new study has found that inebilizumab, a humanized anti-CD19 ...