The Food and Drug Administration has approved Harliku (nitisinone) for the reduction of urine homogentisic acid in adult patients with alkaptonuria.

Alkaptonuria is an ultra-rare hereditary disorder of tyrosine and phenylalanine catabolism, and is commonly known as black urine disease due to the noticeable buildup of HGA. A slow-progressing ...

The Food and Drug Administration (FDA) has approved Harliku ™ (nitisinone) for the reduction of urine homogentisic acid (HGA) in adult patients with alkaptonuria.. Alkaptonuria (AKU) is a rare genetic ...

Oliver Timmis explores the problems associated with securing funding for rare disease research and questions why more funding isn't available in this space. It's difficult to research rare ...

The 1980s initiated a decade of genome cartography. Early maps were based on restriction fragment length polymorphisms (RFLPs) and, in 1987, the first genome-wide map was published. 12 These early ...

The Food and Drug Administration (FDA) has approved an updated label for both chimeric antigen receptor (CAR) T-cell therapies, Breyanzi ® (lisocabtagene maraleucel) and Abecma ® (idecabtagene ...

Harliku becomes the first FDA-approved treatment for alkaptonuria, indicated to reduce homogentisic acid levels in affected adults. FDA Approves Gilead’s Yeztugo as First Twice-Yearly Injection for ...

Find the latest Swedish Orphan Biovitrum AB (publ) (SOBI.ST) stock quote, history, news and other vital information to help you with your stock trading and investing.

Harliku becomes the first FDA-approved treatment for alkaptonuria, indicated to reduce homogentisic acid levels in affected adults. FDA Approves Gilead’s Yeztugo as First Twice-Yearly Injection for ...

The drug was approved for the reduction of urine homogentisic acid in adults with alkaptonuria. Jun 20, 2025 • 2 min read . Study Sheds Light on ...

FDA nod for Cycle Pharma’s Harliku for alkaptonuria . Privately-held UK firm Cycle Pharmaceuticals announced that the US Food and Drug Administration (FDA) has approved Harliku (nitisinone) tablets ...