Columnist Barth Keck takes a look at the words of the year chosen by various dictionary publishers, and offers one of his own.

We flew into St. Barth's airport knowing it would be different. The approach is steep and everything happens fast. Every second requires focus and precision. The runway feels extremely close by the ...

MG was born at term, with birth weight of 2.5 kg, and was discharged with mother after an uneventful perinatal period. He was hospitalized on day 11 because of respiratory difficulty and treated for ...

As the FDA unveils a parade of initiatives aimed at accelerating drug development for rare diseases, experts appeal for a consistent approval process that will support and further catalyze momentum.

The National Organization for Rare Disorders (NORD(R)) today urged Congress to reauthorize the Rare Pediatric Disease Priority Review Voucher (RPD PRV) program by year-end, warning that continued ...

Mast cell activation syndrome is a condition that causes mast cells to release an inappropriate amount of chemicals into your body. This causes allergy symptoms and a wide range of other symptoms.

FORZINITY™ is a mitochondrial cardiolipin binder developed by Stealth BioTherapeutics for the treatment of Barth syndrome. FORZINITY (elamipretide HCl) is indicated for the improvement of muscle ...