Multiple key factors drive the expansion of the Barth syndrome therapeutics market. Firstly, growing awareness of Barth syndrome (a rare genetic disorder) has helped refine the diagnosis and increase ...

Barth syndrome is a rare genetic disorder that mostly affects males and can cause problems with the heart, muscles, and immune system. Common symptoms of Barth syndrome include weak muscles, tiredness ...

NEW YORK, Nov 5 (Reuters) - The U.S. FDA approved a pricey rare disease drug in September despite findings by its data reviewers that the treatment, while safe, was no more effective than a placebo, a ...

Hello! I'm covering the Southtowns for 7 News WKBW. If you have a story idea, please email me at [email protected] BUFFALO, N.Y. (WKBW) — When we celebrate Down Syndrome Awareness Month, advocates ...

(WBNG) - October is Down Syndrome Awareness Month, and here in the Southern Tier, the celebration is going strong. The history of Down Syndrome Awareness Month goes back almost 50 years. “It’s from ...

ALBANY, N.Y. (NEWS10) – October is Down Syndrome Awareness Month. Around 1 in 700 babies in the United States is born each year with Down Syndrome, according to the National Down Syndrome Society.

October marks Down Syndrome Awareness Month, a dedicated period to foster greater understanding, celebrate the lives of individuals with Down syndrome, and advocate for their inclusion in all aspects ...

PRESQUE ISLE, Maine (WAGM) - For three years, a local farmer has been working hard to bring awareness to Down syndrome in the month of October, and he is doing so with Pumpkins, tours, and good ...

Many Faces of Moebius Syndrome celebrates 15 years of global awareness ahead of MSAD 2026, inspiring communities worldwide to share their voices. As we prepare for the 16th Moebius Syndrome Awareness ...

SCRANTON, Pa. — October is Down Syndrome awareness month, and one community laced up their shoes to celebrate in Lackawanna County. The Buddy Walk kicked off at 1:00 p.m. this afternoon at Veterans ...

MOBILE, Ala. (WALA) - Grayson and Erin Allison sit down with Shelby Myers to talk more about Down Syndrome Awareness Month. Shelby and Nicholas share ‘Your Story’ photos Nicholas and Shelby take a ...

After months of fighting, a Colorado family is breathing a sigh of relief after the FDA announced initial approval of an experimental medication helping to keep their son alive. "Like last night, I ...