Researchers attempted to quantify the risk of a catastrophic collision in orbit by coming up with an alarming new metric.

ME/CFS is a neurological condition characterized by malaise. Diagnosis requires ruling out other systemic illnesses.

The meat allergy caused by tick bites was recently linked to the death of a man, who is believed to be the first to die from ...

Multiple key factors drive the expansion of the Barth syndrome therapeutics market. Firstly, growing awareness of Barth syndrome (a rare genetic disorder) has helped refine the diagnosis and increase ...

NEW YORK, Nov 5 (Reuters) - The U.S. FDA approved a pricey rare disease drug in September despite findings by its data reviewers that the treatment, while safe, was no more effective than a placebo, a ...

Background: Barth syndrome (BTHS) is a disorder caused by mutations in the TAFAZZIN gene, which disrupts cardiolipin (CL) metabolism and leads to cardiac and skeletal myopathy, neutropenia, and ...

After months of fighting, a Colorado family is breathing a sigh of relief after the FDA announced initial approval of an experimental medication helping to keep their son alive. "Like last night, I ...

The FDA has granted accelerated approval for the elamipretide injection, the first treatment for Barth syndrome in patients weighing at least 30 kg. Barth syndrome is a life threatening disease of the ...

Cardiomyopathies are often associated with mitochondrial dysfunction. Barth syndrome is a rare, potentially fatal congenital heart disease caused by defects in the mitochondrial enzyme Tafazzin (TAZ) ...

The continued approval of Forzinity is contingent upon verification and description of clinical benefit in a confirmatory trial. The Food and Drug Administration (FDA) has granted accelerated approval ...

After a long regulatory road that included a complete response letter in May, Stealth Biotherapeutics Inc. finally got its Barth syndrome drug across the finish line, with the U.S. FDA granting ...

ORLAND PARK, Ill. (WLS) -- A baby in the Chicago area is battling a rare disease and desperately needs a drug treatment for a better life. The drug has now been granted accelerated approval by the FDA ...