On the very day Noa was diagnosed, an experimental gene therapy and clinical trial were posted to treat Canavan disease. Noa was only the third patient in the world to be dosed with the gene therapy, ...
Friday is Rare Disease Day, which raises awareness for rare diseases and aims to improve access to treatment and medical representation for individuals with rare diseases and their families.
New York’s governor ordered a state school to remove a job posting for a Palestinian studies teaching position this week, ...
MADISON, Wis. (WIFR) - For 14 years, Treyson Wallace’s family searched for answers. Born in 2009, Treyson failed a newborn ...
Growth hormone therapy was initiated for 20 children-14 diagnosed with Turner syndrome and six with GH deficiency-under the ...
Rare Disease Day, observed on Feb. 28, brings attention to uncommon diseases affecting populations of 200,000 or fewer. In ...
A Million Acts of Love (AMAOL) has found their first grantee in Ella Gauthier, a student in Kamloops honouring her brother ...
Feb. 28 is Rare Disease Day. A County mom and dad are sharing their story in hopes of raising awareness of the uncommon ...
WBOY Clarksburg on MSN4h
Buckhannon man raises awareness on Rare Disease DayEvery year since 2008, Rare Disease Day has been held on the last day of February to raise awareness about the research that goes into rare diseases like spinal muscular atrophy (SMA).
Williams, who has performed the National Anthem at baseball stadiums as part of Boehringer Ingelheim’s Breathless campaign, ...
A Lancaster County mother and father are sharing their story in hopes of raising awareness of the uncommon genetic disorder their child is facing. There's no treatment and no cure, but the family is ...
At just 26 months old, Grace Visser was diagnosed with Rett Syndrome, a rare genetic disorder that affects brain development.
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